Nature3 年
First FDA-approved treatment for an ultra-rare disease
Paragangliomas are tumours that arise in the ... Due to their rarity and wide range of non-specific symptoms, these tumours can be very difficult to diagnose. “They’re one of the great medical ...
Nature3 年
The first FDA approved treatment for ultra-rare endocrine tumors
Patients diagnosed with pheochromocytoma or paraganglioma, tumors that form within certain endocrine tissues, such as the adrenal glands, may have abnormal endocrine activity due to the synthesis ...