Columnist Betty Vertin, the mother of three boys with DMD, has the experience and self-assurance to know she can do hard things.

Modalis Therapeutics is seeking to make MDL-101 the first treatment for people with LAMA2-related congenital muscular ...

So we have to change society. It’s a tall order, but it’s been done over and over again throughout history. It starts with a ...

The progression of myotonic dystrophy type 1 (DM1) differs according to sex and age at symptom onset, a four-year follow-up ...

CHMP upheld earlier opinions that Translarna is not of significant benefit to DMD due to nonsense mutations; European ...

Columnist Shalom Lim celebrates a new beginning in a new job, where his mission to serve fellow patients with muscular ...

Usually a DIY project solves a family problem, but columnist Betty Vertin now wonders if her creative efforts contributed to an injury.

Treatment with antimiRs, an RNA-based therapy approach, was able to correct molecular defects in a cell model of myotonic dystrophy type 1 (DM1) — a form of muscular dystrophy — according to the ...

The progression of myotonic dystrophy type 1, known as DM1, differs according to sex and age at symptom onset, according to the findings of a four-year study, but the researchers nonetheless reported ...

The Critical Path Institute (C-Path) is launching a task force to advance the development of therapies for limb-girdle muscular dystrophy (LGMD) and will lead the efforts of its members to find a new ...