This important work examines how microexons contribute to brain activity, structure, and behavior. The authors find that loss of microexon sequences generally has subtle impacts on these metrics in ...

Root-knot nematodes pose a significant threat to agriculture, infecting a wide range of crops and causing billions of dollars ...

This study provides important insights into the regulation of a retained intron in the mRNA coding for OGT, a process known to be regulated by the O-GlcNAc cycling system, and highlights the ...

From placing first in the Sarah Vaughan International Vocal Jazz Competition in 2019 to being a triple Grammy winner, Samara Joy’s rise has been nothing short of meteoric. Joy’s third album, Portrait ...

Stills from Gareth Edwards' Jurassic World: Rebirth is going viral online, drawing varied reactions from many. In these pictures, Jonathan Bailey, Mahershala Ali, and Scarlett Johansson can be seen in ...

Vigeneron GmbH has received IND approval from the FDA for VG-801, a novel mRNA trans-splicing gene therapy to treat Stargardt disease and other retinal dystrophies associated with mutations in the ...

The German gene therapy developer will test VG801 in patients with Stargardt disease and other retinal dystrophies linked with ABCA4 mutations.

Carnegie Mellon’s Joel McManus and Pitt’s Robert Nicholls received a $162,000 grant from the Foundation for Prader-Willi Research to study the regulation and function of a key gene that is usually ...

SpliceBio aims to begin a study testing its protein splicing gene therapy in the first half of 2025, now that the FDA has cleared its IND.

Splicebio S.L. has gained IND clearance from the FDA for its lead program SB-007, a protein splicing gene therapy to address the root genetic cause of Stargardt disease.

A novel study from Korea uncovers the process of synthesis and pivotal role of the transfer RNA-derived fragment, ...